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Study identifier: NCT04256317 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Multi-phase Study of ASTX030 (Azacitidine and Cedazuridine) in Myeloid Neoplasm Alone or in Combination With Venetoclax in AML (AZTOUND Study)

Condition: Myelodysplastic Syndromes · Acute Myeloid Leukemia · Myelodysplastic Syndrome/Neoplasm  ·  Sponsor: Taiho Oncology, Inc.

PhasePhase 2/Phase 3
Planned participants316
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

Study ASTX030-01 is a multi-phase study comprising of Phases 1-3 Monotherapy arms, and Phase 1 and Phase 2 Combination Therapy arms. Phase 1 Monotherapy consists of an open-label Dose Escalation Stage (Stage A) using multiple cohorts at escalating dose levels of oral cedazuridine and azacitidine (only one study drug will be escalated at a time) followed by a Dose Expansion Stage (Stage B). Phase 2 Monotherapy is a randomized, open-label, crossover study to compare oral ASTX030 to subcutaneous (SC) azacitidine. Phase 3 Monotherapy is a randomized open-label crossover study comparing the final fixed dose of oral ASTX030 to SC azacitidine. Phase 1 Combination Therapy is an open-label, multicenter, randomized, exploratory study comparing ASTX030 and SC azacitidine in combination with venetoclax in participants with treatment-naïve AML. Phase 2 Combination Therapy is an open-label, single arm, study evaluating the efficacy, safety, pharmacokinetics (PK), and drug interactions of ASTX030 in combination with venetoclax in participants with treatment-naïve AML. The duration of this multi-phase study is approximately 8 years.

This description comes directly from the study's public registry record.

Talk to the study team

Taiho Oncology, Inc.  ·  +1 844-878-2446  ·  medicalinformation@taihooncology.com

Always discuss trial participation with your own doctor first.

Locations (71)

Keck School of Medicine of USCLos Angeles, California, United StatesRecruiting
UC Irvine Health - Chao Family Comprehensive Cancer CenterOrange, California, United StatesRecruiting
Yale UniversityNew Haven, Connecticut, United StatesRecruiting
University of Miami - Sylvester Comprehensive Cancer CenterMiami, Florida, United StatesRecruiting
University of Emory - Winship Cancer InstituteAtlanta, Georgia, United StatesRecruiting
Dana-Farber Cancer InstituteBoston, Massachusetts, United StatesRecruiting
John Theurer Cancer Center / Hackensack UniversityHackensack, New Jersey, United StatesRecruiting
Roswell Park Comprehensive Cancer CenterBuffalo, New York, United StatesRecruiting
New York University Langone Hospital - Long IslandMineola, New York, United StatesRecruiting
Perlmutter Cancer Center - 34th StreetNew York, New York, United StatesRecruiting
Icahn School of Medicine at Mount SinaiNew York, New York, United StatesRecruiting
Weill Cornell Medical CenterNew York, New York, United StatesWithdrawn

+ 59 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT04256317