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Study identifier: NCT04094610 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Study of Repotrectinib in Pediatric and Young Adult Subjects Harboring ALK, ROS1, OR NTRK1-3 Alterations

Condition: Locally Advanced Solid Tumors · Metastatic Solid Tumors · Lymphoma  ·  Sponsor: Turning Point Therapeutics, Inc.

PhasePhase 1/Phase 2
Planned participants75
Who can joinAll sexes, N/A to 25 Years
Healthy volunteersNo

About this study

Phase 1 will evaluate the safety and tolerability at different dose levels of repotrectinib in pediatric and young adult subjects with advanced or metastatic malignancies harboring anaplastic lymphoma kinase (ALK), receptor tyrosine kinase encoded by the gene ROS1 (ROS1), or neurotrophic receptor kinase genes encoding TRK kinase family (NTRK1-3) alterations to estimate the Maximum Tolerated Dose (MTD) or Maximum Administered Dose (MAD) and select the Pediatric Recommended Phase 2 Dose (RP2D). Phase 2 will determine the anti-tumor activity of repotrectinib in pediatric and young adult subjects with advanced or metastatic malignancies harboring ROS1 or NTRK1-3 alterations.

This description comes directly from the study's public registry record.

Talk to the study team

BMS Study Connect Contact Center www.BMSStudyConnect.com  ·  855-907-3286  ·  Clinical.Trials@bms.com

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Locations (68)

Children's Hospital Los AngelesLos Angeles, California, United StatesRecruiting
University of California at Los AngelesLos Angeles, California, United StatesRecruiting
Children's Hospital Colorado - Anschutz Medical CampusAurora, Colorado, United StatesRecruiting
Local Institution - 2105Orlando, Florida, United StatesCompleted
Local Institution - 2120Orlando, Florida, United StatesCompleted
Children's Healthcare of Atlanta - Egleston HospitalAtlanta, Georgia, United StatesRecruiting
Maine Medical CenterScarborough, Maine, United StatesRecruiting
Dana Farber Cancer Institute.Boston, Massachusetts, United StatesRecruiting
Washington University School of Medicine in St. LouisSt Louis, Missouri, United StatesRecruiting
Local Institution - 2110New Brunswick, New Jersey, United StatesCompleted
Local Institution - 2102New York, New York, United StatesCompleted
Levine Children's Hospital- Pediatric Neuro-OncologyCharlotte, North Carolina, United StatesRecruiting

+ 56 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT04094610