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Study identifier: NCT02074839 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Study of Orally Administered AG-120 in Subjects With Advanced Hematologic Malignancies With an IDH1 Mutation

Condition: Relapsed or Refractory Acute Myeloid Leukemia (AML) · Untreated AML · Other IDH1-mutated Positive Hematologic Malignancies  ·  Sponsor: Institut de Recherches Internationales Servier

PhasePhase 1
Planned participants291
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

The purpose of this Phase I, multicenter study is to evaluate the safety, pharmacokinetics, pharmacodynamics and clinical activity of AG-120 in advanced hematologic malignancies that harbor an IDH1 mutation. The first portion of the study is a dose escalation phase where cohorts of patients will receive ascending oral doses of AG-120 to determine maximum tolerated dose (MTD) and/or the recommended Phase II dose. The second portion of the study is a dose expansion phase where four cohorts of patients will receive AG-120 to further evaluate the safety, tolerability, and clinical activity of the recommended Phase II dose. Additionally, the study includes a substudy evaluating the safety and tolerability, clinical activity, pharmacokinetics, and pharmacodynamics of AG-120 in subjects with relapsed or refractory myelodysplastic syndrome with an IDH1 mutation. Anticipated time on study treatment is until disease progression or unacceptable toxicity occurs.

This description comes directly from the study's public registry record.

Talk to the study team

Institut de Recherches Internationales Servier Clinical Studies Department  ·  +33 1 55 72 43 66  ·  scientificinformation@servier.com

Always discuss trial participation with your own doctor first.

Locations (30)

University of Alabama at BirminghamBirmingham, Alabama, United StatesActive Not Recruiting
Mayo Clinic-AZPhoenix, Arizona, United StatesTerminated
City of HopeDuarte, California, United StatesActive Not Recruiting
University of California-Los AngelesLos Angeles, California, United StatesTerminated
University of California-San FranciscoSan Francisco, California, United StatesTerminated
University of Colorado DenverAurora, Colorado, United StatesTerminated
Mayo Clinic-JacksonvilleJacksonville, Florida, United StatesTerminated
University of MiamiMiami, Florida, United StatesTerminated
Moffit Cancer CenterTampa, Florida, United StatesActive Not Recruiting
Emory UniversityAtlanta, Georgia, United StatesActive Not Recruiting
Northwestern University Medical HospitalChicago, Illinois, United StatesTerminated
John Hopkins Cancer CenterBaltimore, Maryland, United StatesActive Not Recruiting

+ 18 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT02074839