Condition: Gaucher Disease · Cerebroside Lipidosis Syndrome · Glucocerebrosidase Deficiency Disease · Sponsor: Genzyme, a Sanofi Company
The ICGG Gaucher Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with Gaucher disease, irrespective of treatment status. No experimental intervention is involved; patients in the Registry undergo clinical assessments and receive care as determined by the patient's treating physician. The objectives of the Registry are: * To enhance understanding of the variability, progression, identification, and natural history of Gaucher disease, with the ultimate goal of better guiding and assessing therapeutic intervention. * To assist the Gaucher medical community with the development of recommendations for monitoring patients, and to provide reports on patient outcomes, to optimize patient care. * To characterize the Gaucher disease population. * To evaluate the long-term effectiveness of imiglucerase and of eliglustat. Gaucher Pregnancy Sub-registry: The primary objective of this Sub-registry is to track pregnancy outcomes, including complications and infant growth, in all women with Gaucher disease during pregnancy, regardless of whether they receive disease-specific therapy. No experimental intervention is given; thus a patient will undergo clinical assessments and receive standard of care treatment as determined by the patient's physician.If a patient consents to this Sub-registry, information about the patient's medical and obstetric history, pregnancy, and birth will be collected, and, if…
This description comes directly from the study's public registry record.
Trial Transparency email recommended (Toll free number for US & Canada) · 800-633-1610 · contact-us@sanofi.com
ICGG Gaucher Registry HelpLine · +1(617) 252-7500
Always discuss trial participation with your own doctor first.
| Phoenix Children's Hospital- Site Number : 840003 | Phoenix, Arizona, United States | Recruiting |
| University of Arizona- Site Number : 840015 | Tucson, Arizona, United States | Recruiting |
| Arkansas Children's Hospital- Site Number : 840109 | Little Rock, Arkansas, United States | Recruiting |
| University of Arkansas for Medical Sciences- Site Number : 840113 | Little Rock, Arkansas, United States | Recruiting |
| Tower Hematology Oncology Medical Group- Site Number : 840056 | Beverly Hills, California, United States | Recruiting |
| University of California at Irvine- Site Number : 840036 | Irvine, California, United States | Recruiting |
| Southern California Permanente Medical Group- Site Number : 840108 | Los Angeles, California, United States | Recruiting |
| USC Health Sciences Center Dept of Genetics- Site Number : 840082 | Los Angeles, California, United States | Completed |
| Children's Hospital of Orange County- Site Number : 840074 | Orange, California, United States | Recruiting |
| UC Davis MIND Institute- Site Number : 840010 | Sacramento, California, United States | Recruiting |
| Kaiser Permanente Sacramento Medical Center- Site Number : 840042 | Sacramento, California, United States | Completed |
| University of California at San Diego- Site Number : 840007 | San Diego, California, United States | Completed |
+ 306 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT00358943